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tofersen MeSH Supplementary Concept Data 2024


MeSH Supplementary
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Unique ID
C000709090
RDF Unique Identifier
http://id.nlm.nih.gov/mesh/C000709090
Entry Term(s)
BIIB067
Registry Number
2NU6F9601K
Heading Mapped to
*Oligonucleotides
Frequency
7
Note
antisense oligonucleotide that mediates the degradation of superoxide dismutase 1 (SOD1) messenger RNA to reduce SOD1 protein synthesis
Source
N Engl J Med. 2020 Jul 9;383(2):109-119.
Date of Entry
2020/07/28
Revision Date
2022/02/16
tofersen Preferred
BIIB067 Narrower
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