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ataluren MeSH Supplementary Concept Data 2024


MeSH Supplementary
ataluren
Unique ID
C515878
RDF Unique Identifier
http://id.nlm.nih.gov/mesh/C515878
Entry Term(s)
PTC 124
PTC-124
PTC124
Registry Number
K16AME9I3V
Heading Mapped to
*Oxadiazoles
Frequency
168
Note
overrides nonsense stop translation signals to yield full-length proteins; may prove useful in treating cystic fibrosis and Duchenne muscular dystrophy
Source
IDrugs 2006 Nov;9(11):783-9
Date of Entry
2007/01/03
Revision Date
2017/06/27
ataluren Preferred
PTC 124 Narrower
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